Assessing Epidemiological Data Points The findings from this study echo that of another by Trivella and colleagues, also published in Hepatology Communications. This 2023 study is a literature review ...

Prophylactic treatment with cyclophosphamide against graft-versus-host disease following allogeneic hematopoietic stem cell transplantation in patients with myelofibrosis (MF) is “extremely effective, ...

A CRISPR/Cas9-modified Janus kinase 2 (JAK2) V617F model may be useful to develop new therapies against myeloproliferative neoplasms (MPNs), showed a new study published in the International Journal ...

Adult patients with Fabry disease have a lower lean mass compared to healthy people, according to a new study published in the Journal of Rare Diseases. The accumulation of lyso-Gb3 is also correlated ...

Among patients with severe hemophilia A and B, treatment with the monoclonal antibody marstacimab has been associated with reduced rates of bleeding, according to a systemic review and meta-analysis ...

Real-world treatment patterns among newly diagnosed patients with pulmonary arterial hypertension (PAH) have demonstrated low rates of upfront dual-therapy utilization and high rates of ...

There is significant variability in terms of management practices across Canadian medical centers in terms of red blood cell (RBC) and platelet transfusions in preterm newborns, according to a study ...

Megan Garlapow, PhD, is the principal and owner of The Line Medical Communications, LLC, where she brings extensive experience in medical communications across diverse therapeutic areas. Dr Garlapow ...

Sheila Jacobs is the president of STJ Editorial Services. For more than 25 years, Sheila has been providing writing, fact-checking, and editorial services to numerous clients in the medical education, ...

A new case has been reported involving the successful sedation of a patient with cold agglutinin disease (CAD) for an urgent gastroscopy procedure. The report, published in Cureus, reviewed several ...

Phosphodiesterase 3 (PDE3) inhibitors may offer a promising adjunct or alternative approach to enhance skeletal growth in individuals with skeletal dysplasias such as achondroplasia, based on their ...

Patients with Fabry disease appear to have a higher incidence of renal cell carcinoma than the general population, according to a recently published study in Molecular Genetics and Metabolism. “The ...