Muscular dystrophy refers to a group of rare, genetic, progressive diseases that primarily affect the body’s muscles, causing ...

Panelists discuss how data from MDA 2025 demonstrate that delandistrogene moxeparvovec (gene therapy for DMD) shows ...

Another gene therapy death of a Duchenne patient has some parents and doctors criticizing the FDA's actions, even as other ...

U.S. FDA grants Orphan Drug Designation to Deramiocel for the treatment of Becker Muscular Dystrophy, broadening Capricor’s ...

The boys live in Reed City with their mother Tabatha; father Michael, who is the Osceola County Road Commission manager and ...

Another person treated with Elevidys suffered acute liver failure, leading Sarepta to discontinue treatment in certain ...

Shares of Sarepta Therapeutics plunged Monday after the biotech drugmaker reported a second death in connection with its gene ...

Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying ...

Donnacha O’Neill is a happy and outgoing two and a half year old little boy from Meath who loves to be outside and is due to ...

Vader Edwin en zoon Laurens Jan Post uit Breskens doen in juli mee aan de Budapest Rally. Tegelijkertijd willen ze geld ...

[DOORN] Al weken zet Eddy Swart zich in om geld in te zamelen voor Duchenne spierdystrofie. ,,Ik werk bij Monumentenwacht ...